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bioRxiv · 10.1101/2021.10.27.466210

Selective inhibition of PfATP6 by artemisinins and identification of new classes of inhibitors after expression in yeast

Abstract

Treatment failures with artemisinin combination therapies (ACTs) threaten global efforts to eradicate malaria. They highlight the importance of identifying drug targets and new inhibitors and of studying how existing antimalarial classes work. Herein we report the successful development of an heterologous expression-based compound screening tool. Validated drug target P. falciparum calcium ATPase6 (PfATP6) and a mammalian ortholog (SERCA1a) were functionally expressed in yeast providing a robust, sensitive, and specific screening tool. Whole-cell and in vitro assays consistently demonstrated inhibition and labelling of PfATP6 by artemisinins. Mutations in PfATP6 resulted in fitness costs that were ameliorated in the presence of artemisinin derivatives when studied in the yeast model. As previously hypothesised, PfATP6 is a target of artemisinins. Mammalian SERCA1a can be mutated to become more susceptible to artemisinins. The inexpensive, low technology yeast screening platform has identified unrelated classes of druggable PfATP6 inhibitors. Resistance to artemisinins may depend on mechanisms that can concomitantly address multi-targeting by artemisinins and fitness costs of mutations that reduce artemisinin susceptibility.

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BibTeXRIS

Moore, C. M., Wang, J., Lin, Q., Ferreira, P. E., Avery, M. A., Elokely, K., Staines, H. M., Krishna, S.. 2021-10-28. Selective inhibition of PfATP6 by artemisinins and identification of new classes of inhibitors after expression in yeast. https://doi.org/10.1101/2021.10.27.466210

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