@misc{indiciae81f225ee6b0b, title = {KLHL40 gene replacement therapy in severe nemaline myopathy improves survival and skeletal muscle function in a preclinical mouse model}, author = {Tate, G. R. and McNulty, J. and Widrick, J. and Gupta, V. A.}, year = {2026}, doi = {10.64898/2026.09.23.753846}, url = {https://www.biorxiv.org/content/10.64898/2026.09.23.753846v1}, note = {Source identifier: 10.64898/2026.09.23.753846} }