@misc{indiciae10fb3902dcf4, title = {In vivo HSPC gene therapy of hemoglobinopathies without drug selection of corrected cells}, author = {Sakunthala Velmurugan, A. and Paschoudi, K. and Queenan, J. A. and Gil, S. and Maynard, A. and Fontana, C. E. and Sharma, R. and Long, A. and Li, C. and Wang, H. and Anderson, A. K. and Georgakopoulou, A. and Psatha, N. and Giannaki, M. and Vlachaki, E. and Ahmed, N. and Sousa, A. A. and Liu, D. R. and Yannaki, E. and Lieber, A. and Karuppusamy, K. V.}, year = {2026}, doi = {10.64898/2026.09.15.751289}, url = {https://www.biorxiv.org/content/10.64898/2026.09.15.751289v1}, note = {Source identifier: 10.64898/2026.09.15.751289} }