TY - RPRT TI - Targeted mRNA restoration of ciliary function in DNAI1-related primary ciliary dyskinesia: ex vivo rescue in patient-derived nasal spheroids, A pilot study AU - Nygaard, C. M. T. AU - Herrera-Cid, C. R. AU - Nedergaard, L. AU - Johansen, S. G. AU - Matthews, J. G. AU - Couch, J. A. AU - Qvist, T. AU - Nielsen, K. G. AU - Christensen, S. T. AU - Marthin, J. K. PY - 2026 DO - 10.64898/2026.05.26.727937 UR - https://www.biorxiv.org/content/10.64898/2026.05.26.727937v1 ID - 10.64898/2026.05.26.727937 ER -