@misc{indiciaec72a952bbc70, title = {Compact adenine base editors to enable therapeutic rescue of Duchenne muscular dystrophy}, author = {Rallapalli, K. L. and Ho, J. and Nocedal, I. and Tan, J. W. and Ocampo, R. F. and Thomas, N. C. and Justice, B. and Jirde, S. and Gonzalez-Osorio, L. and Castelle, C. J. and Lin, J.-L. and Wright, J. T. and Toch, S. and Shah, K. and Freeman, B. and Rehman, J. and Muysson, J. and Krudop, I. and Alexander, L. M. and Brooks, A. R. and Brown, C. T. and Goltsman, D. S. A. and Hoff, K. G. and Szymanski, P. and Thomas, B. C. and Taylor, D. W. and Butterfield, C. N.}, year = {2026}, doi = {10.64898/2026.05.08.723843}, url = {https://www.biorxiv.org/content/10.64898/2026.05.08.723843v1}, note = {Source identifier: 10.64898/2026.05.08.723843} }