@misc{indiciae3e57fc440472, title = {Cell-autonomous restoration of splicing homeostasis and RP11 phenotype in patient-derived RPE and retinal organoids by PRPF31.AAV gene therapy}, author = {Elia, M. and Pauzuolyte, V. and Georgiou, M. and Basche, M. and Hansohn, C. and Vasconcelos, E. J. R. and Atkinson, R. and Grellscheid, S. and Johnson, C. A. and Hilgen, G. and Urlaub, H. and Smith, A. J. and Mozaffari-Jovin, S. and Ali, R. R. and Lako, M.}, year = {2026}, doi = {10.64898/2026.04.14.718379}, url = {https://www.biorxiv.org/content/10.64898/2026.04.14.718379v1}, note = {Source identifier: 10.64898/2026.04.14.718379} }