@misc{indiciaee03b483963d9, title = {In Utero CFTR Modulation Alleviates Disease in G551D Cystic Fibrosis Pigs}, author = {Ernst, S. E. and Meyerholz, D. K. and Samuel, M. S. and Whitworth, K. M. and Naguib, Y. W. and Nakhla, D. S. and Abou Alaiwa, M. H. and Randak, C. O. and Dong, Q. and Ostedgaard, L. S. and Rehman, T. and Hilkin, B. M. and Powers, L. S. and Stroik, M. R. and Gansemer, N. D. and Rector, M. R. and Taft, P. J. and Hedinger, R. and Goodell, B. J. and Mather, S. E. and Sen, R. and Thornell, I. M. and Bullard, S. A. and Cecil, R. F. and Benne, J. A. and Ash, J. J. and Boyken, L. D. and Karp, P. H. and Tan, P. and Wu, S. and Fischer, A. J. and Cooney, A. L. and Sinn, P. L. and Pezzulo, A. A. and Lee, K. and McCray, P. B. and Zabner, J. and Salem, A. K. and Prather, R. S. and Welsh, M. J. and Stoltz, D. A.}, year = {2026}, doi = {10.64898/2026.01.20.698888}, url = {https://www.biorxiv.org/content/10.64898/2026.01.20.698888v1}, note = {Source identifier: 10.64898/2026.01.20.698888} }