@misc{indiciaef52119a3cf89, title = {Dual-targeting snRNA gene therapy rescues STMN2 and UNC13A splicing in TDP-43 proteinopathies}, author = {Gomberg, T. and Elmsaouri, S. and Kopalle, H. M. and Baughn, M. W. and Beccari, M. S. and McAlonis-Downes, M. and Artates, J. W. and Pant, D. and Mak, H. and Smargon, A. A. and Sander, T. C. and Garcia, E. and Lee, D. P. and Cleveland, D. W. and Yeo, G. W.}, year = {2025}, doi = {10.64898/2025.12.01.691001}, url = {https://www.biorxiv.org/content/10.64898/2025.12.01.691001v1}, note = {Source identifier: 10.64898/2025.12.01.691001} }