@misc{indiciaeba6d0af6aa92, title = {Human iPSC modeling elucidates mutation-specific responses to gene therapy in a genotypically diverse dominant maculopathy}, author = {Sinha, D. and Steyer, B. G. and Shahi, P. K. and Mueller, K. and Valiauga, R. and Edwards, K. L. and Bacig, C. and Steltzer, S. S. and Srinivasan, S. and Abdeen, A. and Cory, E. and Periyasamy, V. and Siahpirani, A. F. and Stone, E. M. and Tucker, B. A. and Roy, S. and Pattnaik, B. R. and Saha, K. and Gamm, D. M.}, year = {2019}, doi = {10.1101/796581}, url = {https://www.biorxiv.org/content/10.1101/796581v1}, note = {Source identifier: 10.1101/796581} }