@misc{indiciaea0a4f7818b50, title = {U7 small nuclear RNA splice-switching therapeutics for STMN2 and UNC13A in Amyotrophic Lateral Sclerosis}, author = {Mehta, P. R. and Solomon, T. and Pickles, S. and Harley, P. and Barioglio, M. and Schweingruber, C. and Marrero-Gagliardi, A. and Gao, Y. and Mattedi, F. and Barattucci, S. and Lin, L. T.-W. and Ryadnov, E. and Zanovello, M. and Cammack, A. J. and Isaacs, A. and Burrone, J. and Shaw, C. E. and Keuss, M. J. and Petrucelli, L. and Fratta, P. and Ruepp, M.-D.}, year = {2025}, doi = {10.1101/2025.11.26.690143}, url = {https://www.biorxiv.org/content/10.1101/2025.11.26.690143v1}, note = {Source identifier: 10.1101/2025.11.26.690143} }