@misc{indiciaecca54b4fb7d9, title = {rAAV-Delivered Bicistronic Artificial microRNAs for Allele-Specific Silencing Improve Motor and Molecular Outcomes in Spinocerebellar Ataxia Type 3}, author = {Silva, A. C. and Henriques, C. and Lobo, D. D. and Fernandes, A. R. and Lopes, M. M. and Leandro, K. and Pereira, D. and Duarte, S. P. and Lopes, S. M. and Santana, M. M. and Dakka, A. and De Marco, S. and Weetall, M. and Narasimhan, J. and Bhattacharyya, A. and Nobre, R. J. and Pereira de Almeida, L.}, year = {2025}, doi = {10.1101/2025.10.02.680011}, url = {https://www.biorxiv.org/content/10.1101/2025.10.02.680011v1}, note = {Source identifier: 10.1101/2025.10.02.680011} }