TY  - RPRT
TI  - Hepatic gene replacement restores energy metabolism and doubles the survival in mouse model of GRACILE syndrome, a neonatal mitochondrial disease
AU  - Banerjee, R.
AU  - Purhonen, J.
AU  - Sultana, N.
AU  - Kietz, C.
AU  - Fellman, V.
AU  - Kallijarvi, J.
PY  - 2025
DO  - 10.1101/2025.09.23.677965
UR  - https://www.biorxiv.org/content/10.1101/2025.09.23.677965v1
ID  - 10.1101/2025.09.23.677965
ER  -