@misc{indiciaee143ab2a394d,
  title = {AAV2-mediated intravitreal delivery of exon-specific U1 snRNA rescues optic neuropathy in a mouse model of familial dysautonomia.},
  author = {Chekuri, A. and Kondabolu, K. and Kirchner, E. G. and Koli, S. and Chagnon, M. and Krasniqi-Vanmeter, D. and Stern, M. E. and Bolduc, J. and Romano, G. and Vandenberghe, L. H. and Morini, E. and Slaugenhaupt, S. A.},
  year = {2025},
  doi = {10.1101/2025.08.21.671454},
  url = {https://www.biorxiv.org/content/10.1101/2025.08.21.671454v1},
  note = {Source identifier: 10.1101/2025.08.21.671454}
}