@misc{indiciaea90841da54a3, title = {Base editing of β0 thalassemia mutations as a therapeutic strategy for β-hemoglobinopathies: efficacy and genotoxicity studies}, author = {Miccio, A. and Hardouin, G. and Martinucci, P. and Scaramuzza, S. and Antoniou, P. and CORRAD, F. and TACHTSIDI, A. and CORRE, G. and MOMBLED, M. and Manceau, S. and Rouillon, C. and Masson, C. and JOSEPH, L. and THURET, I. and NathalY Network, and Allemand, E. and AMENDOLA, M. and Romano, O. and Ferrari, G.}, year = {2025}, doi = {10.1101/2025.08.21.671453}, url = {https://www.biorxiv.org/content/10.1101/2025.08.21.671453v1}, note = {Source identifier: 10.1101/2025.08.21.671453} }