TY  - RPRT
TI  - Systemic neonatal AAV9 gene therapy delivery improves behavioral and phenotypic outcomes comparable to intracerebroventricular delivery in a mouse model of Niemann-Pick disease, type C1
AU  - Epstein, B. E.
AU  - Soden, G. M.
AU  - Incao, A. A.
AU  - Mylvara, A.
AU  - Flynn, J.
AU  - Oszolak, F.
AU  - Pavan, W. J.
PY  - 2025
DO  - 10.1101/2025.08.15.670473
UR  - https://www.biorxiv.org/content/10.1101/2025.08.15.670473v1
ID  - 10.1101/2025.08.15.670473
ER  -