@misc{indiciaec1977569883e, title = {Systemic neonatal AAV9 gene therapy delivery improves behavioral and phenotypic outcomes comparable to intracerebroventricular delivery in a mouse model of Niemann-Pick disease, type C1}, author = {Epstein, B. E. and Soden, G. M. and Incao, A. A. and Mylvara, A. and Flynn, J. and Oszolak, F. and Pavan, W. J.}, year = {2025}, doi = {10.1101/2025.08.15.670473}, url = {https://www.biorxiv.org/content/10.1101/2025.08.15.670473v1}, note = {Source identifier: 10.1101/2025.08.15.670473} }