@misc{indiciae9e5058f98614, title = {Editing of ADA2 Point Mutation in Human Hematopoietic Stem Cells}, author = {Kopcil, P. and Ervik, C. W. and Reint, G. and Mamia, K. and Szymanska, M. and Dahal-Koirala, S. and Conradi, J. and Skjelbostad, S. F. and Donasen, O. A. and Jiang, X. and Fahlquist-Hagert, C. and Kristiansen, O. and Michelsen, T. M. and Melum, E. and Bak, R. O. and Komisarczuk, A. Z. and Haapaniemi, E. M.}, year = {2025}, doi = {10.1101/2025.08.14.670303}, url = {https://www.biorxiv.org/content/10.1101/2025.08.14.670303v1}, note = {Source identifier: 10.1101/2025.08.14.670303} }