@misc{indiciaedac3054e9daa, title = {Antisense oligonucleotides targeting Valosin-containing protein improve muscle pathology and molecular defects in cell and mouse models of multisystem proteinopathy.}, author = {Pal, P. and Carrer, M. and Weiss, L. and Jaime, O. G. and Cheng, C. and Shmara, A. and Boock, V. and Bosch, D. and Youssef, M. and Fazeli, Y. and Afetian, M. and Grossman, T. and Hicks, M. R. and Jafar-nejad, P. and Kimonis, V.}, year = {2025}, doi = {10.1101/2025.07.25.665261}, url = {https://www.biorxiv.org/content/10.1101/2025.07.25.665261v1}, note = {Source identifier: 10.1101/2025.07.25.665261} }