TY  - RPRT
TI  - Antisense oligonucleotide allele-specific targeting of EFEMP1 in a patient-derived model of Doyne honeycomb retinal dystrophy
AU  - Rezek, F. O.
AU  - Sanchez-Pintado, B.
AU  - Eden, E. R.
AU  - Aychoua, N.
AU  - Webster, A. R.
AU  - Carr, A.-J. F.
AU  - Michaelides, M.
AU  - Cheetham, M. E.
AU  - van der Spuy, J.
PY  - 2025
DO  - 10.1101/2025.07.16.664883
UR  - https://www.biorxiv.org/content/10.1101/2025.07.16.664883v1
ID  - 10.1101/2025.07.16.664883
ER  -