@misc{indiciaef64540a1bf4f, title = {Blocking somatic repeat expansion and lowering huntingtin via RNA interference synergize to prevent Huntingtons disease pathogenesis in mice}, author = {Belgrad, J. and Summers, A. and Landles, C. and Greene, J. R. and Hildebrand, S. and Knox, E. and Sapp, E. and Yamada, N. and Furgal, R. and Miller, R. and Osborne, G. F. and Chase, K. and Luu, E. and Freedman, J. and Bramato, B. and McHugh, N. and Benoit, V. and OReilly, D. and Greer, P. and Bates, G. P. and Vogt, T. F. and Lee, R. and Howland, D. and DiFiglia, M. and Aronin, N. and Khvorova, A.}, year = {2025}, doi = {10.1101/2025.06.24.661398}, url = {https://www.biorxiv.org/content/10.1101/2025.06.24.661398v1}, note = {Source identifier: 10.1101/2025.06.24.661398} }