@misc{indiciae4e3a0583f134, title = {Modeling Adeno-Associated Viral Vector 6-mediated In Vivo Gene Delivery to Expanded Non-Mobilized Haemopoietic Stem Cells from Transfusion dependent Thalassemia Patients in a Humanized Mouse}, author = {Ramesh, J. and Kandasamy, K. and Yusof, N. N. and Sujuandy, I. and Keng, C. T. and Chen, L. and Chia, B. S. and Liu, M. and Her, Z. and Kukumberg, M. and Sia, K. C. and Mohd Rodhi, S. H. and Fu, Z. Y. and AJ, R. and Franco-Obregon, A. and Choolani, M. and Sesurajan, B. P. and Lai, P.-S. and Lee, S. Y. and Koh, P. L. and Chen, Q. and Gan, S.-U. and Chew, W. L. and Mattar, C. N.}, year = {2025}, doi = {10.1101/2025.06.17.659025}, url = {https://www.biorxiv.org/content/10.1101/2025.06.17.659025v1}, note = {Source identifier: 10.1101/2025.06.17.659025} }