@misc{indiciae536576568020, title = {Cell modeling and rescue of a novel non-coding genetic cause of Glycogen Storage Disease IX}, author = {Iyengar, A. K. and Zou, X. and Dai, J. and Francis, R. A. and Safi, A. and Patterson, K. and Koch, R. L. and Clarke, S. and Beaman, M. M. and Chong, J. X. and Bamshad, M. J. and Majoros, W. H. and Rehder, R. C. and Bali, D. S. and Allen, A. S. and Crawford, G. E. and Kishnani, P. S. and Reddy, T. E.}, year = {2025}, doi = {10.1101/2025.05.14.654043}, url = {https://www.biorxiv.org/content/10.1101/2025.05.14.654043v1}, note = {Source identifier: 10.1101/2025.05.14.654043} }