@misc{indiciaea5b290c9496b, title = {A systemically delivered AAV-CFTR gene therapy for cystic fibrosis}, author = {Plasschaert, L. W. and Stutz, C. and Otarola, E. and Ruggeri, L. and Misiolek, R. V. and Nuccio, A. and Shang, J. and Choo-Wing, R. and Taddase, B. and Decock, A. and Quigley, C. and Kubek-Luck, K. and Warnant, I. and Aibo, D. I. and Magnifico, M. and Buchs, M. and Tan, G. and Ashley, L. and Wang, H.-K. and Watson, R. and Lin, A.}, year = {2025}, doi = {10.1101/2025.03.20.642115}, url = {https://www.biorxiv.org/content/10.1101/2025.03.20.642115v1}, note = {Source identifier: 10.1101/2025.03.20.642115} }