@misc{indiciae13bd9ff718ac, title = {AAV-mediated ARSA replacement for the treatment of Metachromatic Leukodystrophy}, author = {Ramachandran, S. and Ardinger, J. and Bu, J. and Ramos, M. and Guo, L. and Ghosh, D. and Hossain, M. and Chou, S.-C. and Chen, Y. and Wischof, E. and Ayloo, S. and Trullo, R. and Luo, Y. and Hogestyn, J. and DuBreuil, D. and Crosier, E. and Adams, J. and Richards, A. and Tsabar, M. and Gaglia, G. and Nass, S. and Nambiar, B. and Woodcock, D. and O'Riordan, C. and Tang, Q. and Elmer, B. and Zhang, B. and Goulet, M. and Mueller, C.}, year = {2025}, doi = {10.1101/2025.03.12.642609}, url = {https://www.biorxiv.org/content/10.1101/2025.03.12.642609v1}, note = {Source identifier: 10.1101/2025.03.12.642609} }