@misc{indiciae7d0918f2c3bd, title = {Single-AAV CRISPR editing of skeletal muscle in non-human primates with NanoCas, an ultracompact nuclease}, author = {Rauch, B. J. and DeLoughery, A. and Sper, R. and Chen, S. and Yunanda, S. and Masnaghetti, M. and Chai, N. and Lin, J. C. and Neckelmann, A. and Bjornson, Y. and Espino, D. P. and Sancio, A. and Schmitt, C. and Scholes, C. and Shah, R. and Narendra, P. K. and Ansaloni, S. and Tan, S. and Rukmini, S. J. and Somaiah, S. and Suresh, S. and Minami, S. and Tymoshenko, S. and Wright, W. and Xu, S. and Broughton, J. and Retwitzer, M. D. and Bobbin, M. and Yuan, D. and Abe, K. and DeWitt, M. and Zhang, B. and Harrington, L. B.}, year = {2025}, doi = {10.1101/2025.01.29.635576}, url = {https://www.biorxiv.org/content/10.1101/2025.01.29.635576v1}, note = {Source identifier: 10.1101/2025.01.29.635576} }