@misc{indiciae60a3a233761d, title = {Identifying and treating CLN3 disease outside the central nervous system}, author = {Ziolkowska, E. A. and Jablonka, A. and Williams, L. L. and Jansen, M. J. and Eultgen, E. M. and Wood, M. D. and Hunter, D. A. and Sharma, J. and Sardiello, M. and Sax, S. E. and Bradley, R. P. and Whiteman, I. T. and Reese, R. and Pestronk, A. and Sands, M. S. and Heuckeroth, R. O. and Snyder-Warwick, A. K. and Cooper, J. D.}, year = {2025}, doi = {10.1101/2025.01.29.635518}, url = {https://www.biorxiv.org/content/10.1101/2025.01.29.635518v1}, note = {Source identifier: 10.1101/2025.01.29.635518} }