@misc{indiciae0949528cd188, title = {Targeted Antisense Oligonucleotide Treatment Rescues Developmental Alterations in Spinal Muscular Atrophy Organoids}, author = {Faravelli, I. and Rinchetti, P. and Tambalo, M. and Simutin, I. and Mapelli, L. and Mancinelli, S. and Miotto, M. and Rizzuti, M. and D'Angelo, A. and Cordiglieri, C. and Forotti, G. and Peano, C. and Kunderfranco, P. and Calandriello, L. and Comi, G. P. and Paraboschi, E. and Pali, E. and Beatrice, F. and D'Angelo, E. and Przedborski, S. and Nizzardo, M. and Lodato, S. and Corti, S.}, year = {2025}, doi = {10.1101/2025.01.17.633436}, url = {https://www.biorxiv.org/content/10.1101/2025.01.17.633436v1}, note = {Source identifier: 10.1101/2025.01.17.633436} }