@misc{indiciae58b581d9d920, title = {Lipid-based nanoparticles deliver mRNA to reverse the pathogenesis of lysosomal acid lipase deficiency in a preclinical model}, author = {Zadory, M. and Lopez-Vince, E. and Haddouch, H. and Babity, S. and Rezaei, N. and Moawad, F. and Kenaan El Rahbani, R. M. and Vujic, N. and Kratky, D. and Gravel, S.-P. and Brambilla, D.}, year = {2024}, doi = {10.1101/2024.12.07.627318}, url = {https://www.biorxiv.org/content/10.1101/2024.12.07.627318v1}, note = {Source identifier: 10.1101/2024.12.07.627318} }