TY - RPRT TI - Endothelial and neuronal engagement by AAV-BR1 alleviates neurological symptoms and cholesterol deposition in a mouse model of Niemann-Pick type C2 AU - Rasmussen, C. L. M. AU - Heegaard, C. W. AU - Thomsen, M. S. AU - Hede, E. AU - Laczek, B. AU - Korbelin, J. AU - Thomsen, L. B. AU - Schwaninger, M. AU - Moos, T. AU - Burkhart, A. PY - 2024 DO - 10.1101/2024.04.15.589486 UR - https://www.biorxiv.org/content/10.1101/2024.04.15.589486v1 ID - 10.1101/2024.04.15.589486 ER -