TY  - RPRT
TI  - A blood-brain-barrier penetrant AAV gene therapy rescues neurological deficits in mucolipidosis IV mice.
AU  - Sangster, M.
AU  - Bishop, M.
AU  - Yao, Y.
AU  - Feitor, J. F.
AU  - Shahriar, S.
AU  - Miller, M.
AU  - Chekuri, A.
AU  - Budnik, B.
AU  - Bei, F.
AU  - Grishchuk, Y.
PY  - 2023
DO  - 10.1101/2023.11.03.565568
UR  - https://www.biorxiv.org/content/10.1101/2023.11.03.565568v1
ID  - 10.1101/2023.11.03.565568
ER  -