@misc{indiciaed62c5d682e5f,
  title = {Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations},
  author = {Yoon, J. K. and Schindler, J. W. and Loperfido, M. and Baricordi, C. and DeAndrade, M. P. and Jacobs, M. E. and Treleaven, C. and Plasschaert, R. N. and Yan, A. and Barese, C. N. and Dogan, Y. and Chen, V. P. and Fiorini, C. and Hull, F. and Barbarossa, L. and Unnisa, Z. and Ivanov, D. and Kutner, R. H. and Guda, S. and Oborski, C. and Maiwald, T. and Michaud, V. and Rothe, M. and Schambach, A. and Pfeifer, R. and Mason, C. and Biasco, L. and van Til, N. P.},
  year = {2023},
  doi = {10.1101/2023.11.03.565442},
  url = {https://www.biorxiv.org/content/10.1101/2023.11.03.565442v1},
  note = {Source identifier: 10.1101/2023.11.03.565442}
}