TY - RPRT TI - Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing AU - Hatanaka, F. AU - Suzuki, K. AU - Shojima, K. AU - Yu, J. AU - Takahashi, Y. AU - Sakamoto, A. AU - Prieto, J. AU - Shokhirev, M. AU - Esteban, C. R. AU - Nunez-Delicado, E. AU - Belmonte, J. C. I. PY - 2023 DO - 10.1101/2023.04.06.535786 UR - https://www.biorxiv.org/content/10.1101/2023.04.06.535786v1 ID - 10.1101/2023.04.06.535786 ER -