TY  - RPRT
TI  - CRISPR-Mediated Generation and Characterization of a Gaa Homozygous c.1935C>A (p.D645E) Pompe Disease Knock-in Mouse Model Recapitulates Human Infantile Onset-Pompe Disease
AU  - Kan, S.-h.
AU  - Huang, J. Y.
AU  - Harb, J.
AU  - Rha, A.
AU  - Dalton, N. D.
AU  - Christensen, C.
AU  - Chan, Y.
AU  - Davis-Turak, J.
AU  - Neumann, J.
AU  - Wang, R. Y.
PY  - 2022
DO  - 10.1101/2022.05.30.494061
UR  - https://www.biorxiv.org/content/10.1101/2022.05.30.494061v1
ID  - 10.1101/2022.05.30.494061
ER  -