@misc{indiciaeea0f738ea786, title = {CRISPR/Cas9-Mediated Excision of ALS/FTD-Causing Hexanucleotide Repeat Expansion in C9ORF72 rescues major disease mechanisms in vivo and in vitro}, author = {Meijboom, K. E. and Abdallah, A. and Fordham, N. P. and Nagase, H. and Rodriguez, T. and Kraus, C. and Gendron, T. F. and Krishnan, G. and Esanov, R. and Andrade, N. S. and Rybin, M. J. and Ramic, M. and Stephens, Z. D. and Edraki, A. and Blackwood, M. T. and Kahriman, A. and Henninger, N. and Kocher, J.-P. A. and Benatar, M. and Brodsky, M. H. and Petrucelli, L. and Gao, F.-B. and Sontheimer, E. J. and Brown, R. H. and Zeier, Z. and Mueller, C.}, year = {2022}, doi = {10.1101/2022.05.17.492303}, url = {https://www.biorxiv.org/content/10.1101/2022.05.17.492303v1}, note = {Source identifier: 10.1101/2022.05.17.492303} }