@misc{indiciae8cc5b566ebff, title = {Gene editing is suitable to treat GM1 Gangliosidosis: a proof-of-concept study}, author = {Leclerc, D. and Goujon, L. and Jaillard, S. and Nouyou, B. and Cluzeau, L. and Damaj, L. and Dubourg, C. and Etcheverry, A. and Levade, T. and Froissart, R. and Dreano, S. and Guillory, X. and Eriksson, L. A. and Launay, E. and Mouriaux, F. and Belaud-Rotureau, M.-A. and Odent, S. and Gilot, D.}, year = {2022}, doi = {10.1101/2022.04.17.488473}, url = {https://www.biorxiv.org/content/10.1101/2022.04.17.488473v1}, note = {Source identifier: 10.1101/2022.04.17.488473} }