@misc{indiciae0791b3783ded, title = {mRNA Treatment Rescues Niemann-Pick Disease Type C1 in Patient Fibroblasts}, author = {Furtado, D. and Cortez-Jugo, C. and Hung, Y. H. and Bush, A. I. and Caruso, F.}, year = {2022}, doi = {10.1101/2022.02.21.479058}, url = {https://www.biorxiv.org/content/10.1101/2022.02.21.479058v1}, note = {Source identifier: 10.1101/2022.02.21.479058} }