TY  - RPRT
TI  - Screening of Chimeric GAA Variants in a Preclinical Study of Pompe Disease Results in Candidate Vector for Hematopoietic Stem Cell Gene Therapy
AU  - Dogan, Y.
AU  - Barese, C. N.
AU  - Schindler, J. W.
AU  - Yoon, J. K.
AU  - Unnisa, Z.
AU  - Guda, S.
AU  - Jacobs, M. E.
AU  - Oborski, C.
AU  - Clarke, D. L.
AU  - Schambach, A.
AU  - Pfeifer, R.
AU  - Harper, C.
AU  - Mason, C.
AU  - van Til, N. P.
PY  - 2021
DO  - 10.1101/2021.12.28.474352
UR  - https://www.biorxiv.org/content/10.1101/2021.12.28.474352v1
ID  - 10.1101/2021.12.28.474352
ER  -